Back to top

gene-therapy: Archive

Zacks Equity Research

SRPT Beats on Q3 Earnings & Sales, Discontinues PPMO-Based DMD Program

Sarepta posts encouraging Q3 earnings. After conducting a risk-benefit analysis, the company decides to stop developing the entire PPMO program.

BIIBPositive Net Change FOLDPositive Net Change SRPTNegative Net Change

Zacks Equity Research

CRSP's Q3 Loss Narrower Than Expected, Sales Miss Estimates

CRISPR Therapeutics reports mixed third-quarter results. The commercial launch of the first CRISPR-based gene therapy, Casgevy, is progressing well.

BIIBPositive Net Change VRTXPositive Net Change FOLDPositive Net Change CRSPPositive Net Change

Zacks Equity Research

CRISPR Therapeutics to Report Q3 Earnings: Is a Beat in Store?

On CRSP's third-quarter 2024 earnings call, investors will likely focus on the sales numbers of its recently approved gene therapy, Casgevy.

REGNNegative Net Change PFENegative Net Change VRTXPositive Net Change CRSPPositive Net Change

Zacks Equity Research

EDIT Seeks Partner for Reni-Cel Developmental Program, Stock Down

Editas stock falls on a decision to seek a partner for its lead gene-therapy candidate, reni-cell, for SCD and TDT and focus resources on in vivo pipeline development.

VRTXPositive Net Change ANIPNegative Net Change FATENegative Net Change EDITNegative Net Change

Zacks Equity Research

Pfizer Secures FDA Approval for Hemophilia Drug Hympavzi

Following the FDA approval, PFE's Hympavzi becomes the first hemophilia medicine approved in the United States to be administered via a pre-filled, auto-injector pen.

PFENegative Net Change BMRNNegative Net Change NVONegative Net Change QUREPositive Net Change

Ahan Chakraborty

Fulcrum Stock Tanks 58% in a Month: Buying Opportunity or Risky Bet?

Despite the recent pipeline setback, investors are encouraged to buy the FULC stock based on the potential of its promising SCD candidate, pociredir.

VRTXPositive Net Change CRSPPositive Net Change FULCNegative Net Change

Zacks Equity Research

RARE's Bone Disorder Drug Gets FDA's Breakthrough Therapy Tag

Ultragenyx announces that the FDA grants Breakthrough Therapy designation to its investigational osteogenesis imperfecta treatment candidate, setrusumab.

ALNYNegative Net Change CPRXNegative Net Change ANIPNegative Net Change RARENegative Net Change

Zacks Equity Research

RARE's Wilson Disease Candidate Betters Standard Therapy in Study

Ultragenyx reports superior efficacy of UX701 for Wilson disease compared with standard therapy from the Stage 1 cohorts of its pivotal phase I/II/III study.

ANIPNegative Net Change RARENegative Net Change KRYSPositive Net Change FULCNegative Net Change