Back to top

gene-therapy: Archive

Zacks Equity Research

CRISPR Therapeutics Q4 Earnings and Revenues Surpass Estimates

CRSP reports encouraging fourth-quarter results. The commercial launch of the first CRISPR-based gene therapy, Casgevy, is progressing well.

ALNYPositive Net Change BMRNPositive Net Change VRTXNegative Net Change CRSPPositive Net Change

Zacks Equity Research

RARE Reports New Upbeat Data From Sanfilippo Syndrome Drug Study

Ultragenyx announces new safety and efficacy data from its pivotal study of its investigational candidate, UX111, for patients with Sanfilippo syndrome type A.

ALNYPositive Net Change BMRNPositive Net Change RAREPositive Net Change CSTLNegative Net Change

Sundeep Ganoria

SRPT Stock Rises 23% in a Year: Time to Buy, Hold or Sell?

The upside in Sarepta's share price can be attributed to the encouraging sales performance of its DMD gene therapy, which has demonstrated blockbuster potential.

RHHBYNegative Net Change SRPTPositive Net Change ARWRPositive Net Change

Zacks Equity Research

RARE Submits BLA to the FDA for Sanfilippo Syndrome Gene Therapy

Ultragenyx submits a BLA to the FDA seeking the accelerated approval of UX111 for patients with Sanfilippo syndrome type A in the United States.

RAREPositive Net Change CTMXPositive Net Change SPRONegative Net Change CSTLNegative Net Change

Ekta Bagri

4 Biotech Stocks Most Wall Street Analysts Are Bullish About

Here, we present four biotech stocks, namely SRPT, ADMA, EXEL and ALNY, which most Wall Street analysts are optimistic about. These companies have upside potential for 2025, backed by strong fundamentals.

ALNYPositive Net Change EXELNegative Net Change SRPTPositive Net Change ADMANegative Net Change